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CMT Research Foundation
As the number of gene therapies in trials for CMT continues to grow, how those gene therapies are regulated will become

CMT Research Foundation · 10 posts

Therapies

As the number of gene therapies in trials for CMT continues to grow, how those gene therapies are regulated will becomeAs the number of gene therapies in trials for CMT continues to grow…Jul 1317 likesWe've highlighted the promise of gene therapies in our DEMYSTIFIED webinar series. It concludes on July 16 with a discusWe've highlighted the promise of gene therapies in our DEMYSTIFIED webinar series.Jul 717 likesRegister to learn about how gene therapies are regulated and how you can help shape the future. cmtrf.org/webinarsRegister to learn about how gene therapies are regulated and how you can help shape the…Jul 120 likesGene therapy programs are showing real promise, especially for genetic diseases like CMT. Learn more through our Gene ThGene therapy programs are showing real promise, especially for genetic diseases like CMT.Jun 1751 likesOur GENE THERAPIES DEMYSTIFIED series starts May 7; sign up at cmtrf.org/webinars and bring your questions!Our GENE THERAPIES DEMYSTIFIED series starts May 7…Apr 2353 likesFinding a reliable blood-based marker would make clinical trials more efficient and give doctors a straightforward way tFinding a reliable blood-based marker would make clinical trials more efficient and give…Mar 2726 likesOne of the greatest barriers to developing therapies for Charcot-Marie-Tooth (CMT) disease has been the lack of sensitivOne of the greatest barriers to developing therapies for Charcot-Marie-Tooth (CMT)…Feb 2623 likesThe CMT Research Foundation congratulates NMD Pharma and, above all, the 81 individuals who took part in the Phase 2a SYThe CMT Research Foundation congratulates NMD Pharma and, above all…Feb 337 likesCMTRF funded partner 82VS, the Venture Studio of Alloy Therapeutics, is looking to solve one of the toughest problems inCMTRF funded partner 82VS, the Venture Studio of Alloy Therapeutics…Dec 3, 202513 likesImagine finally getting an answer for the symptoms that have been affecting you for years — only to hear your doctor sayImagine finally getting an answer for the symptoms that have been affecting you for years…Nov 18, 202517 likes

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Country Music Superstar Alan Jackson, who has been open about his diagnosis with CMT, is wrapping up his career with a fCMT Research Foundation EssentialsWe made the 2026 Global CMT Research Convention available for everyone! Browse every talk at cmtconvention.cmtrf.org.CMTRF orgOne of the greatest barriers to developing therapies for Charcot-Marie-Tooth (CMT) disease has been the lack of sensitivCharcot MarieWe made the 2026 Global CMT Research Convention available for everyone! Browse every talk at cmtconvention.cmtrf.org.ConventionThe CMT Research Foundation is launching an innovative fundraising approach for CMT4C. Through the Community Leaders inPatientsThe Zero K Fundraiser Run was a huge success, and we look forward to using the funds for driving CMT research toward a cCure